FDA approves Ultragenyx’s rare disease drug

Ultragenyx Pharmaceutical earned Food and Drug Administration approval for the ultra- rare disease drug Mepsevii.

Advertisement

Mepsevii is an enzyme replacement therapy for patients with Mucopolysaccharidosis VII, an inherited metabolic condition. The disease is extremely rare, affecting an estimated 200 patients globally.

“Prior to today’s approval, patients with this rare, inherited condition had no approved treatment options,” said Julie Beitz, MD, director of the Office of Drug Evaluation III in the FDA’s Center for Drug Evaluation and Research.

Ultragenyx expects Mepsevii to hit the market later this month.

More articles on supply chain: 

Prime Healthcare taps HealthTrust for GPO services
Acorda Therapeutics halts Parkinson’s drug trials after 5 patient deaths
Cardinal Health to sell Chinese distribution business to Shanghai Pharma

Advertisement

Next Up in Supply Chain

  • Medline is laying off 304 workers, according to a notice filed with the state of Illinois and a Nov. 5…

  • As hospitals redefine the role of supply chain leaders to focus on enterprise strategy, digital transformation and resilience, health systems…

Advertisement

Comments are closed.